Special Lunchtime Session: The First Genome-Editing Trial (CCR5)

In this special session, some of the major contributors to the field of genome editing over the last four decades will discuss the first ever genome-editing trial which investigated a zinc finger nuclease for the prevention of HIV.

Confirmed Participants:

Dana Carroll, Ph.D., Distinguished Professor Emeritus, University of Utah School of Medicine, United States

Srinivasan Chandrasegaran, Ph.D., Professor Emeritus, Johns Hopkins School of Public Health, United States

Matthew Porteus, Prof., MD, Ph.D., Stanford Medicine, United States

More details to follow

Special Lunchtime Session: The First Genome-Editing Trial (CCR5)

Panel Discussion: Standards and Regulation in CRISPR Medicine

This one-hour panel discussion will focus on guidance and regulations for gene-editing therapies, lessons learned from the approval CASGEVY, international harmonisation within gene editing, and ensuring safety of gene-editing medicines for all patient groups. Audience participation is welcome.

Confirmed Panelists:

Attila Sebe, MD, PhD (Paul-Ehrlich-Institute, Federal Institute for Vaccines and Biomedicines, Division of Haematology, Cell and Gene Therapy, Germany)

Dolça Rogers, Ph.D., ATMP topic lead, Pharmaceutical Quality Office, European Medicines Agency (EMA), Netherlands

Özcan Met, Ph.D., Associate Professor and Head of Cell Therapy Unit at the National Center for Cancer Immune Therapy (CCIT-DK) at Herlev University Hospital and DTU HealthTech, Denmark

Samantha Maragh, Ph.D., Leader, Genome Editing Program, National Institute of Standards & Technology (NIST), United States

More details to follow

Panel Discussion: Standards and Regulation in CRISPR Medicine

Panel Discussion: Patient Access to CRISPR Medicine

Innovative CRISPR-based therapies hold tremendous promise for addressing a range of diseases, including rare disorders and diseases with unmet medical needs. However, ensuring equitable patient access remains a significant challenge. This one-hour panel discussion will examine key issues involved in the availability and accessibility of CRISPR-based medicines. By bringing together diverse stakeholders, the discussion aims to provide a comprehensive perspective on overcoming barriers to access and ensuring these transformative therapies reach those who need them most. Audience participation is highly encouraged.

Co-organised by Daniël Warmerdam, Ph.D., Assistant Professor, Human Genetics, UMC Amsterdam, Netherlands

Confirmed Partipicants:

Daniël Warmerdam, Ph.D., Assistant Professor, Human Genetics, UMC Amsterdam, Netherlands

Jimi Olaghere, CASGEVY recipient and patient advocate, United States

More details to follow

Panel Discussion: Patient Access to CRISPR Medicine

Special Lunchtime Session: Democratising genetic technologies

This special lunchtime session will discuss strategies to democratise genetic technologies as CRISPR/Cas9 to promote equity in research and personalised medicine approaches derived from those technologies.

More details to follow

Special Lunchtime Session: Democratising genetic technologies