Patient Access

Session co-organiser and moderator: Daniël Warmerdam
Amsterdam UMC, Netherlands
Panelist: Alvin Luk
HuidaGene Therapeutics

Panelist: Cecilia Jimenez-Mallebrera
Institut de Recerca Sant Joan de Déu. Hospital Sant Joan de Déu Barcelona and CIBERER

Panelist: Jimi Olaghere
Patient Advocate

Panelist: Kevin Holden
Synthego

Panelist: Liselotte Wesley Andersen
Rare Diseases Denmark

Panelist: Søren Jarl Christensen
Parent, Founder and CEO of August Foundation (Sammen for August)